SciELO - Brasil - Niemann-Pick disease type C: a case series of

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The aim of the study was to analyze a series of Brazilian patients with Niemann-Pick disease
SciELO - Brasil - Niemann-Pick disease type C: a case series of
Manifestacoes clinicas presentes na doenca de Niemann-Pick tipo c em diferentes faixas etarias: uma revisao da literatura/Clinical manifestations of Niemann-pick type C disease in different age groups: a literature review/Manifestaciones clinicas presentes
SciELO - Brasil - Niemann-Pick disease type C: a case series of
Niemann-Pick disease type C
SciELO - Brasil - Niemann-Pick disease type C: a case series of
Niemann-Pick Disease Type C, A Rare Cause of Pancytopenia: A Case Report
SciELO - Brasil - Niemann-Pick disease type C: a case series of
New variants in Spanish Niemann–Pick type c disease patients
SciELO - Brasil - Niemann-Pick disease type C: a case series of
Frontiers Reproduction in Animal Models of Lysosomal Storage Diseases: A Scoping Review
SciELO - Brasil - Niemann-Pick disease type C: a case series of
Manifestacoes clinicas presentes na doenca de Niemann-Pick tipo c em diferentes faixas etarias: uma revisao da literatura/Clinical manifestations of Niemann-pick type C disease in different age groups: a literature review/Manifestaciones clinicas presentes
SciELO - Brasil - Niemann-Pick disease type C: a case series of
New variants in Spanish Niemann–Pick type c disease patients
SciELO - Brasil - Niemann-Pick disease type C: a case series of
TYPE B NIEMANN-PICK DISEASE: REPORT OF A CASE WITH
SciELO - Brasil - Niemann-Pick disease type C: a case series of
Vaccination strategies for people living with inborn errors of metabolism in Brazil - ScienceDirect
SciELO - Brasil - Niemann-Pick disease type C: a case series of
Niemann-Pick disease type C, Radiology Reference Article
SciELO - Brasil - Niemann-Pick disease type C: a case series of
Patient with Niemann-Pick disease type C: over 20 years' follow-up
SciELO - Brasil - Niemann-Pick disease type C: a case series of
NPC Clinical Severity Scores: Pre-and post-IV infusion. The center
de por adulto (o preço varia de acordo com o tamanho do grupo)